Fighting rare diseases with new methods for clinical trials

The EU-funded INSPIRE project has developed new methods for the design and analysis of clinical trials in rare diseases.

In Europe, nearly 30 million people suffer from a rare disease – or one that effects less than one in 2 000 of the general population. In such settings where numbers are scarce, the large clinical trials typically used to evaluate new drugs and treatments are infeasible – if not impossible. As a result, new approaches for designing such studies, along with improved methods of data analysis, are needed.

Further details: Fighting rare diseases with new methods for clinical trials